News
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PRESS RELEASE
UCSF Benioff Children's Hospitals Become the First US Qualified Treatment Center Contracted to Administer Individualized Gene Therapy WASKYRA®
Fondazione Telethon and Orphan Therapies announce UCSF Benioff Children's Hospitals as the first US Qualified Treatment Center for administering WASKYRA® gene therapy to patients with Wiskott-Aldrich Syndrome (WAS) -
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PRESS RELEASE
Fondazione Telethon Announces FDA approval of Waskyra™ (etuvetidigene autotemcel), a Gene Therapy for the Treatment of Wiskott-Aldrich Syndrome
Fondazione Telethon announces FDA approval of Waskyra gene therapy for Wiskott-Aldrich Syndrome, offering new hope for patients with rare immunodeficiency. Major achievement in rare disease treatment -
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PRESS RELEASE
Fondazione Telethon announces CHMP positive opinion for Waskyra™, a gene therapy for the treatment of Wiskott-Aldrich syndrome (WAS)
Fondazione Telethon receives CHMP positive opinion for Waskyra™ gene therapy treating Wiskott-Aldrich syndrome, advancing rare disease research and patient care
