News
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PRESS RELEASE
Press Release: Sanofi’s venglustat accepted for priority review in the US to treat type 3 Gaucher disease
Sanofi's venglustat granted priority review by FDA for treating type 3 Gaucher disease. Potential first US therapy for neurological manifestations with target action date on November 25, 2026 -
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PRESS RELEASE
Press Release: ATS: phase 2 data demonstrate the superiority of efdoralprin alfa over a standard-of-care augmentation therapy in achieving higher fAAT levels in AATD
ElevAATe phase 2 study shows efdoralprin alfa surpassing traditional therapy in achieving and maintaining fAAT levels in AATD patients with emphysema. Results presented at 2026 ATS International Conference -
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